Pipeline

FIELD CODE CELL TYPE INDICATION DISCOVERY Preclinical Phase I Phase II Phase III
Autoimmune Disease QS-002 Umbilical cord MSC AS

 

ACT-141 CAR-iNK SLE

 

  
ACT-151 CAAR-iNK AS

 

  
Neurological Disease ACT-111 iPS-OPC Spinal Cord Injury

 

ACT-121 iPS-NPC Cerebral Stroke

 

  
ACT-161 Functionally enhanced iOPC* Spinal Cord Injury

 

  
Cancer ACT-131 iNK Liquid Tumor

 

  
ACT-171 CAR-iNK NSCLC

 

  
Respiratory Disease QS-001 Umbilical cord MSC ARDS

 

  
QS-005 Umbilical cord MSC COPD

 

  
Others QS-004 Umbilical cord MSC Liver cirrhosis

 

  
QS-003 Umbilical cord MSC Burns

 

  

Autoimmune Disease

Code Cell Type Indication Phase
QS-002 Umbilical cord MSC AS Phase I
ACT-141 CAR-iNK SLE Discovery
ACT-151 CAAR-iNK AS Discovery

Neurological Disease

Code Cell Type Indication Phase
ACT-111 iPS-OPC Spinal Cord Injury Preclinical
ACT-121 iPS-NPC Cerebral Stroke Preclinical
ACT-161 Functionally enhanced iOPC* Spinal Cord Injury Discovery

Cancer

Code Cell Type Indication Phase
ACT-131 iNK Liquid Tumor Preclinical
ACT-171 CAR-iNK NSCLC Discovery

Respiratory Disease

Code Cell Type Indication Phase
QS-001 Umbilical cord MSC ARDS Phase I
QS-005 Umbilical cord MSC COPD Phase I

Others

Code Cell Type Indication Phase
QS-004 Umbilical cord MSC Liver cirrhosis Phase I
QS-003 Umbilical cord MSC Burns Phase I

AS = Ankylosing Spondylitis   SLE = Systemic Lupus Erythematosus    NSCLC = Non-small Cell Lung Cancer    ARDS = Acute Respiratory Distress Syndrome   

COPD = Chronic Obstructive Pulmonary Disease   iNK = iPS-derived Natural Killer Cells    OPC = Oligodendrocyte Progenitor Cells    NPC = Neural Progenitor Cells

CAAR-iNK = Chimeric Autoantibody Receptor Engineered iNK

* First in class